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Alpha and Beta Thalassemia

Showing 1 - 25 of 8,735

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Alpha-Thalassemia, Alpha Thalassemia Major, Alpha Thalassemia Minor Trial in San Francisco

Recruiting
  • Alpha-Thalassemia
  • +2 more
    • San Francisco, California
      University of California San Francisco
    Oct 7, 2022

    Alpha Thalassemia Major, Hemoglobinopathy; With Thalassemia, Hemoglobinopathies Trial in San Francisco (in utero hematopoietic

    Enrolling by invitation
    • Alpha Thalassemia Major
    • +8 more
    • in utero hematopoietic stem cell transplantation
    • San Francisco, California
      University of California
    Oct 28, 2022

    Human Biospecimens for Basic and Clinical Research Into Globin

    Recruiting
    • Alpha and Beta Thalassemia
    • +3 more
      • Bethesda, Maryland
        National Institutes of Health Clinical Center
      Jan 26, 2023

      Study of the Role of Genetic Modifiers in Hemoglobinopathies

      Recruiting
      • Sickle Cell Disease
      • +3 more
      • GWAS
      • Boston, Massachusetts
      • +24 more
      Apr 4, 2023

      A Single-Site Tissue Repository Providing Annotated Biospecimens

      Recruiting
      • Age-Related Macular Degeneration
      • +46 more
      • Specimen sample
      • Waltham, Massachusetts
        Sanguine Biosciences
      Nov 22, 2022

      Transfusion-dependent Beta-Thalassemia Trial in Peshawar (Thalidomide)

      Completed
      • Transfusion-dependent Beta-Thalassemia
      • Peshawar, Khyber Pakhtunkhwa, Pakistan
        Blood Care Clinic
      Nov 19, 2023

      Non-transfusion-dependent Thalassemia, Low Risk Myelodysplastic Syndrome, Very-Low Risk Myelodysplastic Syndrome Trial in

      Recruiting
      • Non-transfusion-dependent Thalassemia
      • +2 more
      • Düsseldorf, Germany
      • +19 more
      Mar 18, 2022

      Bone Denisty Change in Children With Beta Thalassemia Major

      Not yet recruiting
      • Evaluate Bone Denisty Changes in Children With Beta Thalassemia Major
      • Dexa scan
      • (no location specified)
      Sep 29, 2023

      Thalassemia, Beta, Thalassemia Major Trial in Tianjin (VGB-Ex01)

      Not yet recruiting
      • Thalassemia, Beta
      • Thalassemia Major
      • VGB-Ex01
      • Tianjin, Tianjin, China
        Regenerative Medicine Center
      Sep 11, 2023

      Thalassemia, Beta Trial in Karachi (Hydroxyurea and Thalidomide)

      Completed
      • Thalassemia, Beta
      • Hydroxyurea and Thalidomide
      • Karachi, Sindh, Pakistan
        Children's Hospital Karachi
      Nov 23, 2023

      Screening for Alpha Thalassemia in Healthy Volunteers

      Recruiting
      • Alpha Thalassemia
        • Bethesda, Maryland
          National Institutes of Health Clinical Center
        Jan 26, 2023

        Luspatercept in Korean Myelodysplastic Syndrome or ß-thalassemia

        Not yet recruiting
        • Myelodysplastic Syndrome
        • Beta Thalassemia
        • Seoul, Korea, Republic of
          Bristol-Myers Squibb YH
        Oct 3, 2023

        Transfusion-dependent Beta-thalassemia After Gene Therapy

        Recruiting
        • Transfusion-dependent Beta-Thalassemia
        • Gene Therapy
        • Gene therapy
        • Tianjin, Tianjin, China
          Regenerative Medicine Center
        Aug 6, 2023

        Cognitive Function, Fatigue and Health Related Quality of Life

        Recruiting
        • Cognitive Change
        • +3 more
          • Giza, Egypt
            Abo El-Rish Pediatric Hospital
          Jul 20, 2022

          Atrial Fibrillation in Beta-Thalassemia

          Not yet recruiting
          • Atrial Fibrillation
          • Thalassemia
            • Ferrara, Italy
              Matteo Bertini
            Aug 18, 2022

            ß-thalassemia Trial (BD211)

            Not yet recruiting
            • β-thalassemia
            • BD211
            • (no location specified)
            Mar 15, 2023

            Beta-Thalassemia Trial (CS-101 injection)

            Not yet recruiting
            • Beta-Thalassemia
            • CS-101 injection
            • (no location specified)
            Sep 27, 2023

            Transfusion Dependent Beta Thalassemia, Hemoglobinopathies, Thalassemia Major Trial in Nashville (EDIT-301)

            Recruiting
            • Transfusion Dependent Beta Thalassemia
            • +3 more
            • EDIT-301
            • Oakland, California
            • +3 more
            Jan 3, 2023

            Beta Thalassemia With Increased Tricuspid Regurgitant Jet Velocity Trial in Tanta (L_carnitine, Sildenafil)

            Recruiting
            • Beta Thalassemia With Increased Tricuspid Regurgitant Jet Velocity
            • Tanta, Gharbia, Egypt
              Tanta University Hospital
            Oct 14, 2022

            Pumilio1 Expression, Sickle Cell Anemia, ß-thalassemia

            Not yet recruiting
            • Sickle Cell Disease, Beta Thalassemia Intermedia
            • RNA Binding Protein Pumilio1 (PUM1) Expression by reverse transcriptase quantatative PCR
            • (no location specified)
            May 30, 2023

            Beta-thalassemia Trial in Nanning (Luspatercept, Placebo)

            Recruiting
            • Beta-thalassemia
            • Nanning, China
            • +1 more
            Jan 13, 2023

            Beta-Thalassemia Trial in Nanning (CS-101)

            Recruiting
            • Beta-Thalassemia
            • CS-101
            • Nanning, China
              The First Affiliated Hospital of Guangxi Medical University
            Sep 9, 2023

            Anemia Trial (Luspatercept)

            Not yet recruiting
            • Anemia
            • Luspatercept
            • (no location specified)
            May 26, 2023

            Sickle Cell Anemia, Beta Thalassemia Trial run by the NHLBI (radiation, drug, biological)

            Recruiting
            • Sickle Cell Anemia
            • Beta Thalassemia
            • TBI
            • +6 more
            • Bethesda, Maryland
              National Institutes of Health Clinical Center
            Jan 26, 2023

            Transfusion-dependent Beta-Thalassemia Trial in Tianjin (KL003 cell injection Drug Product)

            Not yet recruiting
            • Transfusion-dependent Beta-Thalassemia
            • KL003 cell injection Drug Product
            • Tianjin, Tianjin, China
              Regenerative Medicine Center
            May 8, 2023