Alpha and Beta Thalassemia
Showing 1 - 25 of 8,735
Alpha-Thalassemia, Alpha Thalassemia Major, Alpha Thalassemia Minor Trial in San Francisco
Recruiting
- Alpha-Thalassemia
- +2 more
-
San Francisco, CaliforniaUniversity of California San Francisco
Oct 7, 2022
Alpha Thalassemia Major, Hemoglobinopathy; With Thalassemia, Hemoglobinopathies Trial in San Francisco (in utero hematopoietic
Enrolling by invitation
- Alpha Thalassemia Major
- +8 more
- in utero hematopoietic stem cell transplantation
-
San Francisco, CaliforniaUniversity of California
Oct 28, 2022
Human Biospecimens for Basic and Clinical Research Into Globin
Recruiting
- Alpha and Beta Thalassemia
- +3 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Jan 26, 2023
Study of the Role of Genetic Modifiers in Hemoglobinopathies
Recruiting
- Sickle Cell Disease
- +3 more
- GWAS
-
Boston, Massachusetts
- +24 more
Apr 4, 2023
A Single-Site Tissue Repository Providing Annotated Biospecimens
Recruiting
- Age-Related Macular Degeneration
- +46 more
- Specimen sample
-
Waltham, MassachusettsSanguine Biosciences
Nov 22, 2022
Transfusion-dependent Beta-Thalassemia Trial in Peshawar (Thalidomide)
Completed
- Transfusion-dependent Beta-Thalassemia
-
Peshawar, Khyber Pakhtunkhwa, PakistanBlood Care Clinic
Nov 19, 2023
Non-transfusion-dependent Thalassemia, Low Risk Myelodysplastic Syndrome, Very-Low Risk Myelodysplastic Syndrome Trial in
Recruiting
- Non-transfusion-dependent Thalassemia
- +2 more
- SLN124
- Placebo
-
Düsseldorf, Germany
- +19 more
Mar 18, 2022
Bone Denisty Change in Children With Beta Thalassemia Major
Not yet recruiting
- Evaluate Bone Denisty Changes in Children With Beta Thalassemia Major
- Dexa scan
- (no location specified)
Sep 29, 2023
Thalassemia, Beta, Thalassemia Major Trial in Tianjin (VGB-Ex01)
Not yet recruiting
- Thalassemia, Beta
- Thalassemia Major
- VGB-Ex01
-
Tianjin, Tianjin, ChinaRegenerative Medicine Center
Sep 11, 2023
Thalassemia, Beta Trial in Karachi (Hydroxyurea and Thalidomide)
Completed
- Thalassemia, Beta
- Hydroxyurea and Thalidomide
-
Karachi, Sindh, PakistanChildren's Hospital Karachi
Nov 23, 2023
Screening for Alpha Thalassemia in Healthy Volunteers
Recruiting
- Alpha Thalassemia
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Jan 26, 2023
Luspatercept in Korean Myelodysplastic Syndrome or ß-thalassemia
Not yet recruiting
- Myelodysplastic Syndrome
- Beta Thalassemia
-
Seoul, Korea, Republic ofBristol-Myers Squibb YH
Oct 3, 2023
Transfusion-dependent Beta-thalassemia After Gene Therapy
Recruiting
- Transfusion-dependent Beta-Thalassemia
- Gene Therapy
- Gene therapy
-
Tianjin, Tianjin, ChinaRegenerative Medicine Center
Aug 6, 2023
Cognitive Function, Fatigue and Health Related Quality of Life
Recruiting
- Cognitive Change
- +3 more
-
Giza, EgyptAbo El-Rish Pediatric Hospital
Jul 20, 2022
Atrial Fibrillation in Beta-Thalassemia
Not yet recruiting
- Atrial Fibrillation
- Thalassemia
-
Ferrara, ItalyMatteo Bertini
Aug 18, 2022
ß-thalassemia Trial (BD211)
Not yet recruiting
- β-thalassemia
- BD211
- (no location specified)
Mar 15, 2023
Beta-Thalassemia Trial (CS-101 injection)
Not yet recruiting
- Beta-Thalassemia
- CS-101 injection
- (no location specified)
Sep 27, 2023
Transfusion Dependent Beta Thalassemia, Hemoglobinopathies, Thalassemia Major Trial in Nashville (EDIT-301)
Recruiting
- Transfusion Dependent Beta Thalassemia
- +3 more
- EDIT-301
-
Oakland, California
- +3 more
Jan 3, 2023
Beta Thalassemia With Increased Tricuspid Regurgitant Jet Velocity Trial in Tanta (L_carnitine, Sildenafil)
Recruiting
- Beta Thalassemia With Increased Tricuspid Regurgitant Jet Velocity
-
Tanta, Gharbia, EgyptTanta University Hospital
Oct 14, 2022
Pumilio1 Expression, Sickle Cell Anemia, ß-thalassemia
Not yet recruiting
- Sickle Cell Disease, Beta Thalassemia Intermedia
- RNA Binding Protein Pumilio1 (PUM1) Expression by reverse transcriptase quantatative PCR
- (no location specified)
May 30, 2023
Beta-Thalassemia Trial in Nanning (CS-101)
Recruiting
- Beta-Thalassemia
- CS-101
-
Nanning, ChinaThe First Affiliated Hospital of Guangxi Medical University
Sep 9, 2023
Anemia Trial (Luspatercept)
Not yet recruiting
- Anemia
- Luspatercept
- (no location specified)
May 26, 2023
Sickle Cell Anemia, Beta Thalassemia Trial run by the NHLBI (radiation, drug, biological)
Recruiting
- Sickle Cell Anemia
- Beta Thalassemia
- TBI
- +6 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Jan 26, 2023
Transfusion-dependent Beta-Thalassemia Trial in Tianjin (KL003 cell injection Drug Product)
Not yet recruiting
- Transfusion-dependent Beta-Thalassemia
- KL003 cell injection Drug Product
-
Tianjin, Tianjin, ChinaRegenerative Medicine Center
May 8, 2023